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FDA Approves First Tablet for SMA Treatment

2/13/2025

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Summary

Story summary

In a groundbreaking move, the FDA has greenlit the first-ever tablet form of risdiplam (Evrysdi) for spinal muscular atrophy (SMA) patients aged 2 and up, who weigh over 44 lbs. This 5 mg tablet can be swallowed whole or dissolved in water, providing the same powerful benefits as its liquid counterpart. Availability is just around the corner!

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Story summary

In a groundbreaking move, the FDA has greenlit the first-ever tablet form of risdiplam (Evrysdi) for spinal muscular atrophy (SMA) patients aged 2 and up, who weigh over 44 lbs. This 5 mg tablet can be swallowed whole or dissolved in water, providing the same powerful benefits as its liquid counterpart. Availability is just around the corner!