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Gene Therapy Restores Sight for 11 Blind Children

3/6/2025

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Summary

Story summary

MeiraGTx has achieved a remarkable breakthrough in gene therapy, restoring sight to 11 children born blind from an AIPL1 gene defect. Surgeons injected the correct gene into their retinas, and within weeks, these children experienced the joy of vision. The company is now seeking regulatory approval in the UK and US, with exciting plans for future therapies.

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Story summary

MeiraGTx has achieved a remarkable breakthrough in gene therapy, restoring sight to 11 children born blind from an AIPL1 gene defect. Surgeons injected the correct gene into their retinas, and within weeks, these children experienced the joy of vision. The company is now seeking regulatory approval in the UK and US, with exciting plans for future therapies.