Story perspectives

Scientists Push for Faster Gene Therapy Development

10/16/2025

Summary

Story summary

Scientists advocate shifting personalized gene-editing therapy development toward streamlined processes and closer collaboration among families, regulators, and researchers.
The Baby KJ case, a recipient of customized CRISPR (clustered regularly interspaced short palindromic repeats) treatment, exemplifies rapid potential in gene therapy.
Fyodor Urnov of the University of California, Berkeley, calls for revived rare-disease programs, increased manufacturing support, and data sharing to accelerate personalized treatments, because children cannot wait.

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Story summary

Scientists advocate shifting personalized gene-editing therapy development toward streamlined processes and closer collaboration among families, regulators, and researchers.
The Baby KJ case, a recipient of customized CRISPR (clustered regularly interspaced short palindromic repeats) treatment, exemplifies rapid potential in gene therapy.
Fyodor Urnov of the University of California, Berkeley, calls for revived rare-disease programs, increased manufacturing support, and data sharing to accelerate personalized treatments, because children cannot wait.