Story perspectives
3-Year-Old First to Receive Groundbreaking Hunter Syndrome Therapy
11/29/2025
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Story summary
- Oliver Chu, a 3-year-old from California, became the first child to receive autologous hematopoietic stem cell gene therapy for Hunter syndrome at Royal Manchester Children's Hospital.
- The therapy replaced the faulty Hunter syndrome gene.
- Three months after treatment, Oliver has shown improvement, with his mother expressing joy.
- Skyler, Oliver's brother, has Hunter syndrome and is too old for this treatment.
- The trial's success raises hopes for therapies for older patients.
