Story perspectives

FDA Rejects Hunter Syndrome Gene Therapy, Families Disappointed

3/5/2026

Summary

Story summary

The U.S. Food and Drug Administration rejected the gene therapy for Hunter syndrome, disappointing many families awaiting treatment.
Megan Selser, whose son has Hunter syndrome, awaits the FDA's decision on the gene therapy she hopes could help him.
Critics point to shifts in the FDA's drug-review process during the Trump administration, including not considering Moderna's flu vaccine, a move some tie to Health Secretary Robert F. Kennedy Jr.'s anti-vaccine stance.

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Story summary

The U.S. Food and Drug Administration rejected the gene therapy for Hunter syndrome, disappointing many families awaiting treatment.
Megan Selser, whose son has Hunter syndrome, awaits the FDA's decision on the gene therapy she hopes could help him.
Critics point to shifts in the FDA's drug-review process during the Trump administration, including not considering Moderna's flu vaccine, a move some tie to Health Secretary Robert F. Kennedy Jr.'s anti-vaccine stance.